Strategic Market Access Planning for Orphan Drugs
By Dr. Paul Craddy & Dr. Graham Foxon
Course Details
Course Details
Treatments for Orphan and Rare Diseases offer attractive business opportunities to pharma, but the path to patient access is paved with many challenges.
To optimise market access, companies need to carefully plan and execute a purposely designed market access strategy, as well as its evidence base and the value proposition.
By attending this 1-day course you will master the critical success factors for developing a strategy and plan, with important lessons learned from many real-life cases.
By participating, you will not only have the chance to ask your specific questions to true Market Access experts, but also experience the unique opportunity to share experiences and engage in in-depth discussions with your international peers.
The current status of payer attitudes and HTAs for orphan drugs.
Guidelines for developing and implementing an optimal market access strategy for orphan drugs: timelines, country customisation, value pricing…
Which evidence you need and how to develop a convincing value proposition that will meet payers’ and regulators’ needs and thus secure timely patient access at a sustainable price.
How Managed Entry Agreements can facilitate patient access.
The benefits and challenges of different types of early access programs.
To see the detailed agenda, please submit your details in the form below the table.
| Welcome & Audience Expectations (~30 min) |
| Opportunities and Challenges from an HTA & Pricing Perspective (~25 min) |
| HTA for Orphan Diseases: Current Practices (~1 h) |
| Framework for Assessing Value of Orphan Drugs (~1 h 20 min) |
| Lunch Break |
| How to Price Rare/Orphan Disease Drugs (~ 30 min) |
| Use of Managed Entry Agreements to Facilitate Patient Access (~30 min) |
| Securing Early Access for Rare Disease Treatments (~30 min) |
| Group Exercise: Developing an Optimal Access Strategy For an Orphan Drug (~1 h) |
| Considerations to Build a Successful Access Strategy for Your Orphan Drug (~30 min) |
| Summary (~15 min) |
| Close |
To see the detailed agenda, please submit your details in the form below:
Dr. Paul Craddy & Dr. Graham Foxon are the founders of Remap Consulting, a specialist pharmaceutical pricing and market access consultancy.
Paul and Graham have supported many pharma companies in developing and implementing pricing and market access strategies, in many instances for rare diseases.
Dr. Paul Craddy's former experience includes global and European pricing and market access positions at Takeda/Nycomed and IMS/Cambridge Pharma.
Dr. Graham Foxon's former market access and pricing experience includes both consultancy at IMS and Adelphi Values, as well as senior positions at GSK, Ferring and a start-up biotech.
Paul and Graham joined CELforPharma’s faculty in 2019. They have a knack for explaining complex matters in a clear and easy to comprehend way. Both are regular guest lecturers at universities and business schools, as well as speakers at international events and conferences.
This course is designed for all managers involved in the process of gaining optimal access of Orphan and Rare Diseases.
If you are a consultant, please contact Annelies Swaan, who will check with the faculty whether you can attend.
Would you like to receive a list of anonymised participant profiles from previous sessions?
Read these testimonials from recent participants:
This course brings structure into an area of many unknowns. Great to have a framework on how to better address them.
UCB
Anke Sieg, GPS Asset Lead, Rare Disease - Belgium - May 2023
Very relevant for anyone with a limited or median level of knowledge in this area. Lots of valuable takeaways that I can implement into my job role, and wonderfully presented by Paul and Graham.
Argenx
Monika Van Den Haute, Regulatory Affairs Director - Belgium - May 2023
Excellent training course led by very knowledgeable trainers! Well worth the time and cost!
Takeda
Mattias Klefbeck, New Product Planning Lead Nordics - Sweden - December 2022
The most beautiful thing about this course is that you can definitely learn new things, no matter whether you already have experience in access or you don't.
SOBI
Marian Marocico, Patient Access and Launch Excellence Lead - Romania - December 2022
The Optimising Access for Orphan and Rare Diseases course was an excellent overview of the market access challenges in the ever-evolving space of rare and orphan diseases. The presenters were very knowledgeable and shared a lot of their experiences in the disease area.
Clinigen Group
Janet Lac, Consulting Associate - United Kingdom - December 2022
28 November 2023, Live online
Early bird € 1 470
(Full fee € 1 670)
(until 27/10/2023)
23 April 2024, Live online
Early bird € 1 470
(Full fee € 1 670)
(until 22/03/2024)
7 November 2024, Live online
Early bird € 1 470
(Full fee € 1 670)
(until 04/10/2024)
Important information:
- Our courses typically take place between 9 AM and 5 PM CET (Brussels, Amsterdam, Paris).
- Live online sessions will be hosted in Zoom.
- Face-to-face courses will take place at a four-star business hotel close to the airport.
- You will receive all practical details after your registration.
For any questions related to the above, please do not hesitate to email Kealeigh Steel or contact her by phone at +32 2 709 01 45.
How to Register
Click the green "Register" button on the course session of your preference.
The registration wizard will guide you through the personal and company data that we need to process your registration.
You have the choice between 2 payment options:
Payment by credit card. You will not be required to pay immediately, but you will receive a secured payment link together with the invoice.
Payment via bank transfer
Click "Register Now". You will be sent an automatic email confirming your registration followed by a personal email containing an invoice and further payment instructions.
For assistance with your registration, please email Kealeigh Steel or contact her by phone at +32 2 709 01 45.
Included in the Registration Fee:
For live online courses:
Access to a virtual small-class (max 20 participants), expert led course in real-time, using an interactive platform for break-out rooms, whiteboard exercises, polling, plenary discussions and chats.
Course material will be provided to you in both digital format (by email) and in hard copy (by post, so you can make notes during the course).
Certificate of attendance signed by the experts and CELforPharma.
VAT Information
The prices on our website are excluding VAT. Depending on the format of the course (face-to-face in Brussels or live online or self-study programme) and your location, we are obliged by Belgian law to apply VAT.
We are obliged by Belgian law to apply VAT in the following cases:
Face-to-Face public course organised in Belgium
Article 53 of the European Union VAT Directive 2006/112 states that : “The place of supply of services in respect of admission to cultural, artistic, sporting, scientific, educational, entertainment or similar events, such as fairs and exhibitions, and of ancillary services related to the admission, supplied to a taxable person, shall be the place where those events actually take place.”
If the course that you register for takes place in Belgium, we are obliged to charge 21% Belgian VAT.
However, you can recover this Belgian VAT through the refund procedure. Note that this procedure differs depending on the country where you are located. It is best to contact your local VAT administration for this.
Online Public courses - live webinar
Webinars where the participants can communicate among themselves or ask questions to the speaker(s) (be it verbally, via a chat function or similar), are considered as ‘online interactive webinars’ by the Belgian VAT administration.
According to Article 53 of the European Union VAT Directive 2006/112, these online interactive webinars take place where the organisation of the seminar takes place, which in this case is Belgium.
So, if you register for one of our live online courses (organised from our offices in Belgium), we are obliged to charge 21% Belgian VAT.
However, you can recover this Belgian VAT through the refund procedure. Note that this procedure differs depending on the country where you are located. It is best to contact your local VAT administration for this.
Self-Study Programme:
A self-study programme is a service provided electronically. It is the period of self-study that is the most important in our self-study Basics of Health Economics and not the kickoff and closing webinars. As a result, this self-study program follows a different VAT application and the place of the service is where the customer is established. Therefore, we follow the VAT rules applicable to the country of your invoicing address.
Group Discounts
Team discounts can be offered to 3 or more delegates from the same company.
Email Annelies Swaan, Director Business Operations, for more details.
Transfer & Cancellation Policy
Flexible Transfer
If a registrant cannot attend the scheduled course, he/she can avoid any cancellation charge by sending a suitable replacement participant.
Alternatively, the registrant can transfer once on a “space available” basis at no extra cost, until 3 weeks prior to the event, to another course of the same value held within one year of the original course date.
Registration Cancellation
Less than 14 days prior to the course date: registrant liable to pay the full invoiced registration fee.
Between 15 and 30 days prior to the course date: registrant liable to pay 50% of the invoiced registration fee.
More than 30 days prior to the course date: registrant liable to pay a cancellation fee of € 450 per registrant.
If a registrant postpones his/her participation to a future course, and cancels again, no refund can be claimed for registration fees.
Benefits of CELforPharma’s face-to-face courses:
You have the unique opportunity to interact 1:1 with the expert(s).
Plenty of opportunity for informal 1:1 and group conversations with your international peers to exchange experiences and ideas, to discuss issues and to network.
Face-to-face interactions allow for more depth during Q&As and group work.
You can step away from your daily routine in the office and enjoy a more focused learning experience in a comfortable business hotel environment.
Benefits of CELforPharma’s live online courses:
The formal programme is as impactful as a face-to-face course thanks to the highly interactive format (using breakouts, polls, quizzes …).
No travel & accommodation expenses
You can attend the course from the comfort of your own office or home.
We send you the course materials by post so that you can take notes and fully engage with the course content.
No, if you choose credit card payment, we will send you a secure payment link together with the invoice.
Team discounts can be offered for 3 or more registrations confirmed at the same time. The level of discount will depend on the number of registrations and the availability of seats.
Email Annelies Swaan, Director Business Operations, for more details.
Depending on the format of the course (face-to-face in Brussels or live online or self-study programme) and your location, we are obliged by Belgian law to apply VAT in the following cases:
Face-to-Face public course organised in Belgium
Article 53 of the European Union VAT Directive 2006/112 states that : “The place of supply of services in respect of admission to cultural, artistic, sporting, scientific, educational, entertainment or similar events, such as fairs and exhibitions, and of ancillary services related to the admission, supplied to a taxable person, shall be the place where those events actually take place.”
If the course that you register for takes place in Belgium, we are obliged to charge 21% Belgian VAT.
However, you can recover this Belgian VAT through the refund procedure. Note that this procedure differs depending on the country where you are located. It is best to contact your local VAT administration for this.
Online Public courses - live webinar
Webinars where the participants can communicate among themselves or ask questions to the speaker(s) (be it verbally, via a chat function or similar), are considered as ‘online interactive webinars’ by the Belgian VAT administration.
According to Article 53 of the European Union VAT Directive 2006/112, these online interactive webinars take place where the organisation of the seminar takes place, which in this case is Belgium.
So, if you register for one of our live online courses (organised from our offices in Belgium), we are obliged to charge 21% Belgian VAT.
However, you can recover this Belgian VAT through the refund procedure. Note that this procedure differs depending on the country where you are located. It is best to contact your local VAT administration for this.
Self-Study Programme:
A self-study programme is a service provided electronically. It is the period of self-study that is the most important in our self-study Basics of Health Economics and not the kickoff and closing webinars. As a result, this self-study program follows a different VAT application and the place of the service is where the customer is established. Therefore, we follow the VAT rules applicable to the country of your invoicing address.
Our face-to-face courses in Brussels and Zurich take place in four-star business hotels close to the airport. As part of our strong relationship with these hotels, CELforPharma has secured a discount on the daily room rate for our delegates who book their accommodation via us.
Upon your registration, we will assist you to make your hotel booking. For any assistance in this matter please do not hesitate to email Kealeigh Steel, Senior Programme Coordinator, or contact her by phone at +32 2 709 01 45.
We do not record our live online public courses as we want to offer a safe environment for all attendees to share their experiences and freely ask questions.
This way, by participating in our courses, you do not only learn from our expert faculty but also from your international peers in the room.
No, we don't sell the course materials as a stand-alone.
Without the expert's explanation, the exercises and the discussions with other course participants, there is very little value in the slides.
Email Inge Cornelis, partner with CELforPharma, to help you choose the course that is best suited.
Yes!
We have helped many managers with setting up an in-house training programme for their team.
Email Inge Cornelis, partner with CELforPharma, to discuss your team training needs.
Do you have any other questions?
Email Annelies Swaan or call +32 486 98 52 49.
People attending this course are typically also interested in:
By clicking the below button, you will save this course to MY COURSES in the upper right corner of the website. This allows you to quickly retrieve it later.
Don’t forget to make a personal account using the Login button in the upper right corner of the website to keep your list of saved courses for your next visit.
Upcoming Session
28 November 2023, Live online
Early bird € 1 470
(Full fee € 1 670)
(until 27/10/2023)
Treatments for Orphan and Rare Diseases offer attractive business opportunities to pharma, but the path to patient access is paved with many challenges.
To optimise market access, companies need to carefully plan and execute a purposely designed market access strategy, as well as its evidence base and the value proposition.
By attending this 1-day course you will master the critical success factors for developing a strategy and plan, with important lessons learned from many real-life cases.
By participating, you will not only have the chance to ask your specific questions to true Market Access experts, but also experience the unique opportunity to share experiences and engage in in-depth discussions with your international peers.
The current status of payer attitudes and HTAs for orphan drugs.
Guidelines for developing and implementing an optimal market access strategy for orphan drugs: timelines, country customisation, value pricing…
Which evidence you need and how to develop a convincing value proposition that will meet payers’ and regulators’ needs and thus secure timely patient access at a sustainable price.
How Managed Entry Agreements can facilitate patient access.
The benefits and challenges of different types of early access programs.
To see the detailed agenda, please submit your details in the form below the table.
| Welcome & Audience Expectations (~30 min) |
| Opportunities and Challenges from an HTA & Pricing Perspective (~25 min) |
| HTA for Orphan Diseases: Current Practices (~1 h) |
| Framework for Assessing Value of Orphan Drugs (~1 h 20 min) |
| Lunch Break |
| How to Price Rare/Orphan Disease Drugs (~ 30 min) |
| Use of Managed Entry Agreements to Facilitate Patient Access (~30 min) |
| Securing Early Access for Rare Disease Treatments (~30 min) |
| Group Exercise: Developing an Optimal Access Strategy For an Orphan Drug (~1 h) |
| Considerations to Build a Successful Access Strategy for Your Orphan Drug (~30 min) |
| Summary (~15 min) |
| Close |
To see the detailed agenda, please submit your details in the form below:
Dr. Paul Craddy & Dr. Graham Foxon are the founders of Remap Consulting, a specialist pharmaceutical pricing and market access consultancy.
Paul and Graham have supported many pharma companies in developing and implementing pricing and market access strategies, in many instances for rare diseases.
Dr. Paul Craddy's former experience includes global and European pricing and market access positions at Takeda/Nycomed and IMS/Cambridge Pharma.
Dr. Graham Foxon's former market access and pricing experience includes both consultancy at IMS and Adelphi Values, as well as senior positions at GSK, Ferring and a start-up biotech.
Paul and Graham joined CELforPharma’s faculty in 2019. They have a knack for explaining complex matters in a clear and easy to comprehend way. Both are regular guest lecturers at universities and business schools, as well as speakers at international events and conferences.
This course is designed for all managers involved in the process of gaining optimal access of Orphan and Rare Diseases.
If you are a consultant, please contact Annelies Swaan, who will check with the faculty whether you can attend.
Would you like to receive a list of anonymised participant profiles from previous sessions?
Read these testimonials from recent participants:
This course brings structure into an area of many unknowns. Great to have a framework on how to better address them.
UCB
Anke Sieg, GPS Asset Lead, Rare Disease - Belgium - May 2023
Very relevant for anyone with a limited or median level of knowledge in this area. Lots of valuable takeaways that I can implement into my job role, and wonderfully presented by Paul and Graham.
Argenx
Monika Van Den Haute, Regulatory Affairs Director - Belgium - May 2023
Excellent training course led by very knowledgeable trainers! Well worth the time and cost!
Takeda
Mattias Klefbeck, New Product Planning Lead Nordics - Sweden - December 2022
The most beautiful thing about this course is that you can definitely learn new things, no matter whether you already have experience in access or you don't.
SOBI
Marian Marocico, Patient Access and Launch Excellence Lead - Romania - December 2022
The Optimising Access for Orphan and Rare Diseases course was an excellent overview of the market access challenges in the ever-evolving space of rare and orphan diseases. The presenters were very knowledgeable and shared a lot of their experiences in the disease area.
Clinigen Group
Janet Lac, Consulting Associate - United Kingdom - December 2022
28 November 2023, Live online
Early bird € 1 470
(Full fee € 1 670)
(until 27/10/2023)
23 April 2024, Live online
Early bird € 1 470
(Full fee € 1 670)
(until 22/03/2024)
7 November 2024, Live online
Early bird € 1 470
(Full fee € 1 670)
(until 04/10/2024)
Important information:
- Our courses typically take place between 9 AM and 5 PM CET (Brussels, Amsterdam, Paris).
- Live online sessions will be hosted in Zoom.
- Face-to-face courses will take place at a four-star business hotel close to the airport.
- You will receive all practical details after your registration.
For any questions related to the above, please do not hesitate to email Kealeigh Steel or contact her by phone at +32 2 709 01 45.
How to Register
Click the green "Register" button on the course session of your preference.
The registration wizard will guide you through the personal and company data that we need to process your registration.
You have the choice between 2 payment options:
Payment by credit card. You will not be required to pay immediately, but you will receive a secured payment link together with the invoice.
Payment via bank transfer
Click "Register Now". You will be sent an automatic email confirming your registration followed by a personal email containing an invoice and further payment instructions.
For assistance with your registration, please email Kealeigh Steel or contact her by phone at +32 2 709 01 45.
Included in the Registration Fee:
For live online courses:
Access to a virtual small-class (max 20 participants), expert led course in real-time, using an interactive platform for break-out rooms, whiteboard exercises, polling, plenary discussions and chats.
Course material will be provided to you in both digital format (by email) and in hard copy (by post, so you can make notes during the course).
Certificate of attendance signed by the experts and CELforPharma.
VAT Information
The prices on our website are excluding VAT. Depending on the format of the course (face-to-face in Brussels or live online or self-study programme) and your location, we are obliged by Belgian law to apply VAT.
We are obliged by Belgian law to apply VAT in the following cases:
Face-to-Face public course organised in Belgium
Article 53 of the European Union VAT Directive 2006/112 states that : “The place of supply of services in respect of admission to cultural, artistic, sporting, scientific, educational, entertainment or similar events, such as fairs and exhibitions, and of ancillary services related to the admission, supplied to a taxable person, shall be the place where those events actually take place.”
If the course that you register for takes place in Belgium, we are obliged to charge 21% Belgian VAT.
However, you can recover this Belgian VAT through the refund procedure. Note that this procedure differs depending on the country where you are located. It is best to contact your local VAT administration for this.
Online Public courses - live webinar
Webinars where the participants can communicate among themselves or ask questions to the speaker(s) (be it verbally, via a chat function or similar), are considered as ‘online interactive webinars’ by the Belgian VAT administration.
According to Article 53 of the European Union VAT Directive 2006/112, these online interactive webinars take place where the organisation of the seminar takes place, which in this case is Belgium.
So, if you register for one of our live online courses (organised from our offices in Belgium), we are obliged to charge 21% Belgian VAT.
However, you can recover this Belgian VAT through the refund procedure. Note that this procedure differs depending on the country where you are located. It is best to contact your local VAT administration for this.
Self-Study Programme:
A self-study programme is a service provided electronically. It is the period of self-study that is the most important in our self-study Basics of Health Economics and not the kickoff and closing webinars. As a result, this self-study program follows a different VAT application and the place of the service is where the customer is established. Therefore, we follow the VAT rules applicable to the country of your invoicing address.
Group Discounts
Team discounts can be offered to 3 or more delegates from the same company.
Email Annelies Swaan, Director Business Operations, for more details.
Transfer & Cancellation Policy
Flexible Transfer
If a registrant cannot attend the scheduled course, he/she can avoid any cancellation charge by sending a suitable replacement participant.
Alternatively, the registrant can transfer once on a “space available” basis at no extra cost, until 3 weeks prior to the event, to another course of the same value held within one year of the original course date.
Registration Cancellation
Less than 14 days prior to the course date: registrant liable to pay the full invoiced registration fee.
Between 15 and 30 days prior to the course date: registrant liable to pay 50% of the invoiced registration fee.
More than 30 days prior to the course date: registrant liable to pay a cancellation fee of € 450 per registrant.
If a registrant postpones his/her participation to a future course, and cancels again, no refund can be claimed for registration fees.
Benefits of CELforPharma’s face-to-face courses:
You have the unique opportunity to interact 1:1 with the expert(s).
Plenty of opportunity for informal 1:1 and group conversations with your international peers to exchange experiences and ideas, to discuss issues and to network.
Face-to-face interactions allow for more depth during Q&As and group work.
You can step away from your daily routine in the office and enjoy a more focused learning experience in a comfortable business hotel environment.
Benefits of CELforPharma’s live online courses:
The formal programme is as impactful as a face-to-face course thanks to the highly interactive format (using breakouts, polls, quizzes …).
No travel & accommodation expenses
You can attend the course from the comfort of your own office or home.
We send you the course materials by post so that you can take notes and fully engage with the course content.
No, if you choose credit card payment, we will send you a secure payment link together with the invoice.
Team discounts can be offered for 3 or more registrations confirmed at the same time. The level of discount will depend on the number of registrations and the availability of seats.
Email Annelies Swaan, Director Business Operations, for more details.
Depending on the format of the course (face-to-face in Brussels or live online or self-study programme) and your location, we are obliged by Belgian law to apply VAT in the following cases:
Face-to-Face public course organised in Belgium
Article 53 of the European Union VAT Directive 2006/112 states that : “The place of supply of services in respect of admission to cultural, artistic, sporting, scientific, educational, entertainment or similar events, such as fairs and exhibitions, and of ancillary services related to the admission, supplied to a taxable person, shall be the place where those events actually take place.”
If the course that you register for takes place in Belgium, we are obliged to charge 21% Belgian VAT.
However, you can recover this Belgian VAT through the refund procedure. Note that this procedure differs depending on the country where you are located. It is best to contact your local VAT administration for this.
Online Public courses - live webinar
Webinars where the participants can communicate among themselves or ask questions to the speaker(s) (be it verbally, via a chat function or similar), are considered as ‘online interactive webinars’ by the Belgian VAT administration.
According to Article 53 of the European Union VAT Directive 2006/112, these online interactive webinars take place where the organisation of the seminar takes place, which in this case is Belgium.
So, if you register for one of our live online courses (organised from our offices in Belgium), we are obliged to charge 21% Belgian VAT.
However, you can recover this Belgian VAT through the refund procedure. Note that this procedure differs depending on the country where you are located. It is best to contact your local VAT administration for this.
Self-Study Programme:
A self-study programme is a service provided electronically. It is the period of self-study that is the most important in our self-study Basics of Health Economics and not the kickoff and closing webinars. As a result, this self-study program follows a different VAT application and the place of the service is where the customer is established. Therefore, we follow the VAT rules applicable to the country of your invoicing address.
Our face-to-face courses in Brussels and Zurich take place in four-star business hotels close to the airport. As part of our strong relationship with these hotels, CELforPharma has secured a discount on the daily room rate for our delegates who book their accommodation via us.
Upon your registration, we will assist you to make your hotel booking. For any assistance in this matter please do not hesitate to email Kealeigh Steel, Senior Programme Coordinator, or contact her by phone at +32 2 709 01 45.
We do not record our live online public courses as we want to offer a safe environment for all attendees to share their experiences and freely ask questions.
This way, by participating in our courses, you do not only learn from our expert faculty but also from your international peers in the room.
No, we don't sell the course materials as a stand-alone.
Without the expert's explanation, the exercises and the discussions with other course participants, there is very little value in the slides.
Email Inge Cornelis, partner with CELforPharma, to help you choose the course that is best suited.
Yes!
We have helped many managers with setting up an in-house training programme for their team.
Email Inge Cornelis, partner with CELforPharma, to discuss your team training needs.
Do you have any other questions?
Email Annelies Swaan or call +32 486 98 52 49.
People attending this course are typically also interested in:
By clicking the below button, you will save this course to MY COURSES in the upper right corner of the website. This allows you to quickly retrieve it later.
Don’t forget to make a personal account using the Login button in the upper right corner of the website to keep your list of saved courses for your next visit.